Despite a long-held reputation as a relatively mild party drug, nitrous oxide is becoming increasingly dangerous and building ...
Federal health officials are investigating a Salmonella outbreak linked to recalled Rosabella Moringa Capsules that sickened ...
The Food and Drug Administration aims to evaluate treatments for rare diseases based on plausible evidence that they would work — without requiring a clinical trial first.
How innovative technologies like AI and gene editing are advancing rare disease drug discovery and development.
Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced the U.S. Food and Drug Administration (FDA or the Agency) has ...
Some tuberculosis program managers report double-digit increases, and the cost of antibiotics to treat it is rising.
PharmAla Biotech Holdings Inc. (CSE: MDMA)(OTCQB: MDXXF), a biotechnology company focused on the research, development, and ...
New Program Designed as Platform-based Approach for Direct Correction of Mutations Causing PKU; Investigational New Drug (IND) Filing for ...
Preeclampsia is a serious, potentially fatal high blood pressure disorder that can develop during or after pregnancy. It affects between 5% and 8% of pregnancies.
VTVT stock outlook: underfollowed T1D catalyst with Phase 3 CATT1 cadisegliatin data due 2H2026, improved timeline and runway ...
PDUFA action date set for August 23, 2026 If approved, DTX401 will be the first treatment to address the underlying cause of GDSIa NOVATO, Calif., Feb. 23, 2026 (GLOBE NEWSWIRE) -- Ultragenyx Pharmace ...
Boehringer Ingelheim acquires an exclusive license for a preclinical oral immunology program from Sitryx in a deal worth over ...
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