In honor of Rare Disease Day, columnist Halsey Blocher shines a light on the caregivers who make life possible for those with SMA.
The first patient has been dosed in a Phase 1/2 study of GB221, a next-generation gene therapy for SMA type 1.
Medical equipment and technology are crucial for columnist Ari Anderson, who lives with SMA, so malfunctions can quickly ...
Blood vessel damage in the spinal cord may play a role in nerve cell loss in spinal muscular atrophy, a new study suggests.
Columnist Helen Baldwin recalls the major life changes that preceded her introduction to the SMA community with the birth of ...
Columnist Connie Chandler enjoys volunteer work, but her physical limitations from SMA means she often needs a little help ...
A mouse study suggests SMA treatment may partly restore organ-specific redox imbalances linked to SMN protein deficiency.
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